Spark Therapeutics, Inc.;The Children's Hospital of Philadelphia
发明人:
HIGH, Katherine A.,DAVIDSON, Beverly L.
申请号：
EP17847658
公开号：
EP3506930A4
申请日:
2017.09.01
申请国别(地区):
EP
年份:
2020
代理人:
摘要：
Methods and uses of treating a disease in a mammal are provided by administering to a mammalian non-central nervous system (CNS) cell, organ or tissue, for delivery to mammalian CNS (e.g., brain). Methods and uses of treating a disease in a mammal include, inter alia, administering to a mammalian non-ocular cell, organ or tissue for delivery to a mammalian ocular cell, organ or tissue.
