SPARK THERAPEUTICS, INC.; INC.;SPARK THERAPEUTICS;THE CHILDREN'S HOSPITAL OF PHILADELPHIA
发明人:
HIGH, KATHERINE A.,DAVIDSON, BEVERLY L.
申请号：
CA3035628
公开号：
CA3035628A1
申请日:
2017.09.01
申请国别(地区):
CA
年份:
2018
代理人:
摘要：
Methods and uses of treating a disease in a mammal are provided by administering to a mammalian non-central nervous system (CNS) cell, organ or tissue, for delivery to mammalian CNS (e.g., brain). Methods and uses of treating a disease in a mammal include, inter alia, administering to a mammalian non-ocular cell, organ or tissue for delivery to a mammalian ocular cell, organ or tissue.
