ESTEVE PHARMACEUTICALS, S.A.;UNIVERSITAT AUTÒNOMA DE BARCELONA
发明人:
申请号:
PT16730716
公开号:
PT3303576T
申请日:
2016.06.03
申请国别(地区):
PT
年份:
2020
代理人:
摘要:
The present invention provides new Adeno-associated virus-derived vectors and pharmaceutical compositions containing the same for the treatment of lysosomal storage disorders and specially, for the treatment of mucopolysaccharidoses Type II.