ESTEVE PHARMACEUTICALS, S.A.;UNIVERSITAT AUTÓNOMA DE BARCELONA
发明人:
Carles ROCA LECHA,Virginia A. HAURIGOT-MENDONÇA,Fàtima BOSCH TUBERT
申请号：
US16337953
公开号：
US20190231900A1
申请日:
2017.09.22
申请国别(地区):
US
年份:
2019
代理人:
摘要：
The present invention provides new adeno-associated virus-derived vectors and pharmaceutical compositions containing the same for the treatment of lysosomal storage disorders and specially, for the treatment of mucopolysaccharidoses Type IIID.
