SCHEMAS POSOLOGIQUES COMPRENANT (3R, 4R, 5S)-5-(DIFLUOROMETHYL)PIPERIDINE-3,4-DIOL POUR LE TRAITEMENT ET LA PREVENTION DE TROUBLES LYSOSOMIAUX ET DE TROUBLES DEGENERATIFS DU SYSTEME NERVEUX CENTRAL

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专利权人:

INC.;AMICUS THERAPEUTICS

发明人:

CLARK, SEAN

申请号：

CA2996428

公开号：

CA2996428A1

申请日:

2016.08.31

申请国别(地区):

CA

年份:

2017

代理人:

摘要：

Described herein are dosing regimens and kits comprising (3R, 4R, 5S)-5-(difluoromethyl)piperidine-3.4-diol for the treatment and/or prevention of lysosomal storage disorders such as Gaucher disease. Also described are dosing regimens and kits comprising (3R, 4R, 5S)-5-(difluoromethyl)piperidine-3.4-diol for the treatment and/or prevention of degenerative disorders of the central nervous system, such as the synucleinopathies Parkinson's disease or Lewy Body Dementia.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/