A regimen comprising (3R, 4R, 5S) -5- (difluoromethyl) piperidine-3,4-diol for the treatment and prevention of lysosomal disorders and degenerative disorders of the central nervous system
Dosage regimens and kits comprising (3R, 4R, 5S) -5- (difluoromethyl) piperidine-3,4-diol for the treatment and / or prevention of lysosomal storage disorders (such as Gaucher disease) are described herein. Described in. (3R, 4R, 5S) -5- (difluoromethyl) piperidine-3,4 for the treatment and / or prevention of degenerative disorders of the central nervous system (such as synucleinopathic Parkinson's disease or Lewy body dementia) -Dosing regimens and kits containing diols are also described. [Selection] Figure 1リソソーム貯蔵障害(ゴーシェ病等)の治療及び/または予防のための(3R,4R,5S)-5-(ジフルオロメチル)ピペリジン-3,4-ジオールを含む、投薬レジメン及びキットが、本明細書において記載される。中枢神経系の変性障害(シヌクレイノパチーのパーキンソン病またはレビー小体型認知症等)の治療及び/または予防のための(3R,4R,5S)-5-(ジフルオロメチル)ピペリジン-3,4-ジオールを含む、投薬レジメン及びキットも記載される。【選択図】図1