Regimens comprising (3R, 4R, 5S) -5- (difluoromethyl) piperidine-3,4-diol to treat and prevent lysosomal disorders and degenerative disorders of the central nervous system
- 专利权人:
- Amicus Therapeutics; Inc.
- 发明人:
- CLARK, Sean
- 申请号:
- ES16767076
- 公开号:
- ES2781969T3
- 申请日:
- 2016.08.31
- 申请国别(地区):
- ES
- 年份:
- 2020
- 代理人:
- 摘要:
- Described herein are dosing regimens and kits for the treatment and/or prevention of lysosomal storage disorders such as Gaucher disease. Also described are dosing regimens and kits for the treatment and/or prevention of degenerative disorders of the central nervous system, such as the synucleinopathies Parkinson's disease or Lewy Body Dementia.
- 来源网站:
- 中国工程科技知识中心
相关发明人
相关专利
- Regimens comprising (3R, 4R, 5S)-5-(difluoromethyl)piperidine-3.4-diol for treating and preventing lysosomal disorders and degenerative disorders of the central nervous system
- A regimen comprising (3R, 4R, 5S) -5- (difluoromethyl) piperidine-3,4-diol for the treatment and prevention of lysosomal disorders and degenerative disorders of the central nervous system
- Compounds for preventing and/or treating lysosomal storage disorders and/or degenerative disorders of the central nervous system
- Novel compounds for preventing and/or treating lysosomal storage disorders and/or degenerative disorders of the central nervous system
- Novel Compounds For Preventing And/Or Treating Lysosomal Storage Disorders And/Or Degenerative Disorders Of The Central Nervous System