OLIGONUCLEOTIDES DE COMMUTATION OU DE MODULATION D'EPISSAGE DE PRE-ARNM COMPRENANT DES FRAGMENTS D'ECHAFAUDAGE BICYCLIQUES, PRESENTANT DES CARACTERISTIQUES AMELIOREES POUR LE TRAITEMENT DES TROUBLES D'ORIGINE GENETIQUE
VAN DEUTEKOM, JUDITH CHRISTINA THEODORA,DE VISSER, PETER CHRISTIAN
申请号：
CA3029772
公开号：
CA3029772A1
申请日:
2017.07.05
申请国别(地区):
CA
年份:
2018
代理人:
摘要：
The current invention provides antisense splice-switching oligonucleotides with improved characteristics that enhance clinical applicability for treating, ameliorating, preventing, and/or delaying neuromuscular disorders, such as DMD.
