KABADI, AMI MEDA,COWAN, CHAD ALBERT,LUNDBERG, ANTE SVEN
申请号：
CA3000931
公开号：
CA3000931A1
申请日:
2016.10.28
申请国别(地区):
CA
年份:
2017
代理人:
摘要：
The present application provides materials and methods for treating a patient with Duchenne Muscular Dystrophy (DMD) both ex vivo and in vivo. In addition, the present application provides materials and methods for editing a dystrophin gene in a cell by genome editing.
