BIKALUTAMIDO ANALOGAI ARBA (S)-BIKALUTAMIDAS, KAIP EGZOCITOZĘ AKTYVUOJANTYS JUNGINIAI, SKIRTI LIZOSOMINIO KAUPIMO SUTRIKIMO ARBA GLIKOGENOZĖS GYDYMUI

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专利权人:

BCN Peptides; S.A.

发明人:

FARRERA-SINFREU, Josep,MATALONGA BORREL, Leslie,GORT MAS, Laura,PASCUAL MARTINEZ, Roberto,FERRER MONTIEL, Antonio,RIBES RUBIO, Antonia,PONSATI OBIOLS, Berta

申请号：

LT14815747

公开号：

LT3086784T

申请日:

2014.12.19

申请国别(地区):

LT

年份:

2019

代理人:

摘要：

SUMMARY The invention provides a therapy for lysosomal storage diseases and glycogenosis by treatment with compounds that promote exocytosis, preferably lysosomal exocytosis. The treatment of cells from patients affected by different lysosomal storage disorders with exocytosis activating compounds leads to a decrease in the accumulation of toxic substrate in the lysosomes, thus allowing the treatment, prevention and relief of the symptoms of many lysosomal storage disorders.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/