METHODS AND COMPOSITIONS FOR THE TREATMENT OF LYSOSOMAL STORAGE DISEASES
- 专利权人:
- 发明人:
- 申请号:
- EP13715059.5
- 公开号:
- EP2872625A1
- 申请日:
- 2013.03.15
- 申请国别(地区):
- EP
- 年份:
- 2015
- 代理人:
- 摘要:
- Nucleases and methods of using these nucleases for inserting a sequence encoding a therepeutic protein such as an enzyme into a cell, thereby providing proteins or cell therapeutics for treatment and/or prevention of a lysosomal storage disease.
- 来源网站:
- 中国工程科技知识中心
相关发明人
相关专利
- Methods and compositions for the treatment of lysosomal storage diseases
- METHODS AND COMPOSITIONS FOR THE TREATMENT OF LYSOSOMAL STORAGE DISEASES
- METHODS AND COMPOSITIONS FOR THE TREATMENT OF LYSOSOMAL STORAGE DISEASES
- Methods and compositions for the treatment of lysosomal storage diseases
- Treatment of proteinopathies