LABORATORIOS DEL DR. ESTEVE S.A.;UNIVERSITAT AUTONOMA DE BARCELONA
发明人:
BOSCH TUBERT, M FATIMA,HAURIGOT MENDOCA, M VIRGINIA,RIBERA SANCHEZ, ALBERT
申请号:
CA2947468
公开号:
CA2947468A1
申请日:
2015.05.13
申请国别(地区):
CA
年份:
2015
代理人:
摘要:
The present invention provides new adenoassociated virus vectors and pharmaceutical compositions containing the same for the treatment of lysosomal storage disorders and specially, for the treatment of mucopolysaccharidoses Type IIIB.