Laboratorios del Dr. ESTEVE S.A.;Universitat Autònoma de Barcelona
发明人:
M Fàtima BOSCH TUBERT,M Virginia HAURIGOT MENDOÇA,Albert RIBERA SANCHEZ
申请号:
US15310524
公开号:
US20170088859A1
申请日:
2015.05.13
申请国别(地区):
US
年份:
2017
代理人:
摘要:
The present invention provides new adenoassociated virus vectors and pharmaceutical compositions containing the same for the treatment of lysosomal storage disorders and specially, for the treatment of mucopolysaccharidoses Type IIIB.