AUPEPIN DE LAMOTHE-DREUZY, EDOUARD,CHANG, KAIHSIN,SANCHEZ, MINERVA ELAINE,HEATH, JACK
申请号:
CA3093289
公开号:
CA3093289A1
申请日:
2019.03.07
申请国别(地区):
CA
年份:
2019
代理人:
摘要:
Genome editing systems, guide RNAs, and CRISPR-mediated methods are provided for altering portions of the HBG1 and HBG2 loci in cells and increasing expression of fetal hemoglobin.