Systems and methods for the treatment of hemoglobinopathies
- 专利权人:
- Editas Medicine; Inc.
- 发明人:
- GORI, Jennifer Leah,AUPEPIN DE LAMOTHE-DREUZY, Edouard,HEATH, Jack
- 申请号：
- AU2019234922
- 公开号：
- AU2019234922A1
- 申请日:
- 2019.03.14
- 申请国别(地区):
- AU
- 年份:
- 2020
- 代理人:
- 摘要：
- Genome editing systems, guide RNAs, and CRISPR-mediated methods are provided for altering portions of the HBG1 and HBG2 loci in cells and increasing expression of fetal hemoglobin.
- 来源网站：
- 中国工程科技知识中心
