COMPOSÉ D'ACIDE BENZOÏQUE 1,2,4-OXADIAZOLE ET SON UTILISATION POUR LA SUPPRESSION NON-SENS ET LE TRAITEMENT DE MALADIES
- 专利权人:
- PTC Therapeutics; Inc.
- 发明人:
- 申请号:
- EP17153046.2
- 公开号:
- EP3178816A1
- 申请日:
- 2004.04.09
- 申请国别(地区):
- EP
- 年份:
- 2017
- 代理人:
- 摘要:
- Provided herein is a compound of formula (I):for use in a method of treating cystic fibrosis resulting from a premature stop codon in a patient.
- 来源网站:
- 中国工程科技知识中心
相关发明人
相关专利
- COMPOSÉ D'ACIDE BENZOÏQUE 1,2,4-OXADIAZOLE ET SON UTILISATION POUR LA SUPPRESSION NON-SENS ET LE TRAITEMENT DE MALADIES
- TREATMENT OF CYSTIC FIBROSIS BY DELIVERY OF CODON-OPTIMIZED mRNA ENCODING CFTR
- Treatment of cystic fibrosis by delivery of codon-optimized mrna encoding CFTR
- TREATMENT OF CYSTIC FIBROSIS BY DELIVERY OF CODON-OPTIMIZED mRNA CODING CFTR
- Novel codon-optimized CFTR mRNA