Research Institute at Nationwide Children's Hospital
发明人:
HARPER, Scott Quenton
申请号：
EP17776877
公开号：
EP3435755A4
申请日:
2017.03.31
申请国别(地区):
EP
年份:
2019
代理人:
摘要：
The present invention relates to a tissue-specific promoter system for expressing microRNA (miRNA) for RNA interference-based methods of gene therapy. In these systems, the miRNA will inhibit gene expression or replace natural miRNA expression using microRNA.
