RESEARCH INSTITUTE AT NATIONWIDE CHILDREN'S HOSPITAL
发明人:
Scott Quenton Harper
申请号：
US16651814
公开号：
US20200248179A1
申请日:
2018.10.02
申请国别(地区):
US
年份:
2020
代理人:
摘要：
The present disclosure relates to a tissue-specific promoter system for expressing microRNA (miRNA) for RNA interference-based methods of gene therapy. In these systems, the miRNA will inhibit gene expression or replace natural miRNA expression using microRNA.
