RESEARCH INSTITUTE AT NATIONWIDE CHILDREN'S HOSPITAL;RESEARCH INSTITUTE AT NATIONWIDE CHILDRENS HOSPITAL
发明人:
HARPER, SCOTT QUENTON
申请号：
CA3019832
公开号：
CA3019832A1
申请日:
2017.03.31
申请国别(地区):
CA
年份:
2017
代理人:
摘要：
The present invention relates to a tissue-specific promoter system for expressing microRNA (miRNA) for RNA interference-based methods of gene therapy. In these systems, the miRNA will inhibit gene expression or replace natural miRNA expression using microRNA.
