RESEARCH INSTITUTE AT NATIONWIDE CHILDREN'S HOSPITAL;RESEARCH INSTITUTE AT NATIONWIDE CHILDRENS HOSPITAL
发明人:
RODINO-KALAPAC, Louise,POTTER, Rachael
申请号：
SG11201804166Y
公开号：
SG11201804166YA
申请日:
2016.11.15
申请国别(地区):
SG
年份:
2018
代理人:
摘要：
The present application provides materials and methods for treating a patient with a titin-based myopathy, particularly a titin-based cardiomyopathy, and/or other titinopathy. In addition, the present application provides materials and methods for editing the titin gene in a cell by genome editing.
