Materials and Methods for Treatment of Titin-Based Myopathies and other Titinopathies

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专利权人:

发明人:

Louise Rodino-Klapac,Rachael Potter

申请号：

US15776714

公开号：

US20180360921A1

申请日:

2016.11.15

申请国别(地区):

US

年份:

2018

代理人:

摘要：

The present application provides materials and methods for treating a patient with a titin-based myopathy, particularly a titin-based cardiomyopathy, and/or other titinopathy. In addition, the present application provides materials and methods for editing the titin gene in a cell by genome editing.

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中国工程科技知识中心

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http://www.ckcest.cn/home/