Van Bree, Johannes, Brenardus, Mathias, Marie,Venneker, Edna, Henriette, Germaine,Meeker, David, P.
申请号:
EP20080164825
公开号:
EP2020438(B1)
申请日:
1999.12.06
申请国别(地区):
欧洲专利局
年份:
2018
代理人:
摘要:
The invention provides methods of treating Pompe's disease using human acid alpha glucosidase. A preferred treatment regime comprises administering greater than 10mg/kg body weight per week to a patient.