Ying YANG,Chad Albert COWMAN,Ante Sven LUNDBERG,Gregory Joseph COST
申请号:
US15999370
公开号:
US20190112353A1
申请日:
2017.17.02
申请国别(地区):
US
年份:
2019
代理人:
摘要:
Materials and methods for treating a patient with severe combined immunodeficiency (SCID) or Omenn Syndrome, both ex vivo and in vivo, and materials and methods for editing to modulate the expression, function, or activity of an lnterleukin-7 receptor (IL7R) gene in a cell by genome editing.