University of Florida Research Foundation; Incorporated
发明人:
Manuela Corti,Barry John Byrne
申请号：
US16745962
公开号：
US20200138975A1
申请日:
2020.01.17
申请国别(地区):
US
年份:
2020
代理人:
摘要：
Provided herein are nucleic acids, recombinant adeno-associated viral particles, compositions and methods related to treating Friedreich's ataxia. In some examples, the nucleic acids, recombinant adeno-associated viral particles, compositions and methods involve us of a FXN coding sequence, a truncated FXN 3′； UTR, and a prompter.
