RESEARCH INSTITUTE AT NATIONWIDE CHILDREN'S HOSPITAL
发明人:
Louise RODINO-KLAPAC,Jerry R. MENDELL
申请号：
MX2018012604
公开号：
MX2018012604A
申请日:
2017.04.14
申请国别(地区):
MX
年份:
2019
代理人:
摘要：
The invention provides for recombinant AAV vectors comprising a miniaturized human micro-dystrophin gene and methods of using the recombinant vectors to reduce or prevent fibrosis in subjects suffering from muscular dystrophy.La invención proporciona vectores AAV recombinantes que comprenden un gen de microdistrofina humana miniaturizado y métodos para usar los vectores recombinantes para reducir o prevenir la fibrosis en sujetos que padecen distrofia muscular.
