SEYMOUR, Albert Barnes,AHMED, Seemin Seher,WRIGHT, Jason Boke,DOLLIVE, Serena Nicole,MCSWIGGEN, James Anthony,PROUT, Jaime Michelle,SOOKIASIAN, Danielle Lauren
申请号：
AU2019215152
公开号：
AU2019215152A1
申请日:
2019.02.01
申请国别(地区):
AU
年份:
2020
代理人:
摘要：
Provided herein are adeno-associated virus (AAV) compositions that can restore phenylalanine hydroxylase (PAH) gene function in cell. Also provided are methods of use of the AAV compositions, and packaging systems for making the AAV compositions.
