Albert Barnes Seymour,Seemin Seher Ahmed,Jason Boke Wright,Serena Nicole Dollive,James Anthony McSwiggen,Jaime Michelle Prout,Danielle Lauren Sookiasian
申请号：
US16265684
公开号：
US20190256867A1
申请日:
2019.02.01
申请国别(地区):
US
年份:
2019
代理人:
摘要：
Provided herein are adeno-associated virus (AAV) compositions that can restore phenylalanine hydroxylase (PAH) gene function in cell. Also provided are methods of use of the AAV compositions, and packaging systems for making the AAV compositions.
