Rubén Darío ARTERO ALLEPUZ,Ariadna BARGIELA SCHÖNBRUNN,Beatriz LLAMUSÍ TROÍSI,Manuel PÉREZ ALONSO,Juan Manuel FERNÁNDEZ COSTA
申请号：
US15537346
公开号：
US20180263943A1
申请日:
2015.12.18
申请国别(地区):
US
年份:
2018
代理人:
摘要：
Compound for treatment of myotonic dystrophy type The present invention relates to a compound, or a salt thereof, and a pharmaceutical composition comprising said compound, or a salt thereof, for use in the prevention and/or treatment of myotonic dystrophy type 1 in a patient, in particular by reducing the levels of autophagy and apoptosis that are elevated in myotonic muscular dystrophy type 1.
