ARTERO ALLEPUZ, RUBEN DARIO,BARGIELA SCHONBRUNN, ARIADNA,LLAMUSI TROISI, BEATRIZ,PEREZ ALONSO, MANUEL,FERNANDEZ COSTA, JUAN MANUEL
申请号:
CA2971369
公开号:
CA2971369A1
申请日:
2015.12.18
申请国别(地区):
CA
年份:
2016
代理人:
摘要:
Compound for treatment of myotonic dystrophy type The present invention relates to a compound, or a salt thereof, and a pharmaceutical composition comprising said compound, or a salt thereof, for use in the prevention and/or treatment of myotonic dystrophy type 1 in a patient, in particular by reducing the levels of autophagy and apoptosis that are elevated in myotonic muscular dystrophy type 1.