Methods and compositions for treating hemophilia
- 专利权人:
- Sangamo Therapeutics; Inc.
- 发明人:
- Jeffrey C. Miller,David Paschon,Edward J. Rebar
- 申请号：
- US15673163
- 公开号：
- US10407476B2
- 申请日:
- 2017.08.09
- 申请国别(地区):
- US
- 年份:
- 2019
- 代理人:
- 摘要：
- Disclosed herein are methods and compositions for insertion of transgene sequences encoding proteins involved in clotting into the genome of a cell for treating conditions including hemophilias.
- 来源网站：
- 中国工程科技知识中心
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