MILLER, Jeffrey C.,PASCHON, David,REBAR, Edward J.,WECHSLER, Thomas,ZHANG, Lei
申请号:
DK14869719
公开号:
DK3080274T3
申请日:
2014.12.09
申请国别(地区):
DK
年份:
2020
代理人:
摘要:
Disclosed herein are methods and compositions for insertion of transgene sequences encoding proteins involved in clotting into the genome of a cell for treating conditions including hemophilias.