METHODS AND COMPOSITIONS FOR MODIFICATION OF A CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR (CFTR) GENE
- 专利权人:
- Sangamo Therapeutics; Inc.
- 发明人:
- Anthony Conway
- 申请号:
- US16607605
- 公开号:
- US20200079826A1
- 申请日:
- 2018.05.02
- 申请国别(地区):
- US
- 年份:
- 2020
- 代理人:
- 摘要:
- Nucleases and methods of using these nucleases for alteration of a CFTR gene and generation of cells and animal models.
- 来源网站:
- 中国工程科技知识中心
相关发明人
相关专利
- METHODS AND COMPOSITIONS FOR ALTERATION OF A CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR (CFTR) GENE
- METHODS AND COMPOSITIONS FOR ALTERATION OF A CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR (CFTR) GENE
- Methods and compositions for alteration of a cystic fibrosis transmembrane conductance regulator (CFTR) gene
- Methods and compositions for modification of the cystic fibrosis transmembrane conductance regulator (CFTR) gene
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