Methods and compositions for the treatment of HuntingtonS disease

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专利权人:

Michael Hayden

发明人:

Michael Hayden,Jeffrey Carroll,Simon Warby

申请号：

US12991883

公开号：

US08679750B2

申请日:

2009.05.08

申请国别(地区):

US

年份:

2014

代理人:

摘要：

Methods and compositions for reducing expression of a mutant huntingtin (mHTT) protein in a cell are provided. Such methods include contacting the cell with an effective amount of a nucleic acid silencing agent targeting a differentiating polymorphism in RNA encoding the mHTT.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/