University of Rochester;Fred Hutchinson Cancer Research Center;Leiden University Medical Center
发明人:
申请号：
EP16191567.3
公开号：
EP3192880A1
申请日:
2011.08.18
申请国别(地区):
EP
年份:
2017
代理人:
摘要：
The invention provides an agent capable of inhibiting or suppressing the level of DUX4-fl expression in a population of cells in a mammalian subject, for use in a method of treating a mammalian subject suffering from, or at risk for developing, Facioscapulohumeral Dystrophy (FSHD), wherein the agent is a nucleic acid.
