UNIVERSITY OF ROCHESTER;SNIDER, LAUREN;FRED HUTCHINSON CANCER RESEARCH CENTER;LEIDEN UNIVERSITY MEDICAL CENTER
发明人:
SNIDER, LAUREN,VAN DER MAAREL, SILVERE, M.,TAPSCOTT, STEPHEN, J.,TAWIL, RABI,LEMMERS, RICHARD, J.L.F.,GENG, LINDA
申请号：
EP11818806
公开号：
EP2606152A4
申请日:
2011.08.18
申请国别(地区):
EP
年份:
2014
代理人:
摘要：
The invention provides an agent capable of inhibiting or suppressing the level of DUX4-fl expression in a population of cells in a mammalian subject, for use in a method of treating a mammalian subject suffering from, or at risk for developing, Facioscapulohumeral Dystrophy (FSHD), wherein the agent is a nucleic acid.
