FRANK DEROSA,MICHAEL HEARTLEIN,CHARLES GUILD BRAYDON
申请号:
PT12728007
公开号:
PT2717893T
申请日:
2012.06.08
申请国别(地区):
PT
年份:
2019
代理人:
摘要:
Disclosed herein are compositions and methods for modulating the production of a protein in a target cell. The compositions and methods disclosed herein are capable of ameliorating diseases associated with protein or enzyme deficiencies.