DAILEY, Vernon,CHAKIATH, Marion,ZHANG, Shyuan,MASLOWSKI, John,MALYALA, Anna
申请号：
SG11201807893Q
公开号：
SG11201807893QA
申请日:
2017.03.16
申请国别(地区):
SG
年份:
2018
代理人:
摘要：
The present invention relates to self-inactivating lentiviral vectors comprising the COL7A1 gene or a functional variant thereof and its use in a method for the treatment of Type VII collagen deficiency, such as dominant dystrophic epidermolysis and recessive dystrophic epidermolysis.
