DAILEY, VERNON,CHAKIATH, MARION,ZHANG, SHYUAN,MASLOWSKI, JOHN,MALYALA, ANNA
申请号：
CA3017757
公开号：
CA3017757A1
申请日:
2017.03.16
申请国别(地区):
CA
年份:
2017
代理人:
摘要：
The present invention relates to self-inactivating lentiviral vectors comprising the COL7A1 gene or a functional variant thereof and its use in a method for the treatment of Type VII collagen deficiency, such as dominant dystrophic epidermolysis and recessive dystrophic epidermolysis.
