Cornell University;INSERM (Institut National de la S;Centre National De La Recherche Scientifique (CNRS);Université Paris-Sud XI;APHP (Assistance Publique - Hôpitaux de Paris);Université de Strasbourg
发明人:
PUCCIO, Helene Monique,AUBOURG, Patrick,CRYSTAL, Ronald G.,BOUGNERES, Pierre
申请号：
AU2018202783
公开号：
AU2018202783A1
申请日:
2018.04.20
申请国别(地区):
AU
年份:
2018
代理人:
摘要：
#$%^&*AU2018202783A120180524.pdf#####Abstract The present invention relates to a method for preventing or treating cardiomyopathy due to energy failure in a subject in need thereof, comprising administering to said subject a therapeutically effective amount of a vector which comprises a nucleic acid sequence of a gene that can effectively restore energy. More particularly, the method relates to cardiomyopathy associated with Friedrich ataxia and wherein the vector comprises a fraxtaxin (FXN) encoding nucleic acid.
