PUCCIO HÉLÈNE MONIQUE,AUBOURG PATRICK,CRYSTAL RONALD G,BOUGNERES PIERRE
申请号：
IN7071/DELNP/2015
公开号：
IN2015DN07071A
申请日:
2015.08.12
申请国别(地区):
IN
年份:
2015
代理人:
摘要：
The present invention relates to a method for preventing or treating cardiomyopathy due to energy failure in a subject in need thereof comprising administering to said subject a therapeutically effective amount of a vector which comprises a nucleic acid sequence of a gene that can restore energy failure. More particularly the invention relates to a method for preventing or treating a cardiomyopathy associated with Friedreich ataxia in a subject in need thereof comprising administering to said subject a therapeutically effective amount of a vector which comprises a frataxin (FXN) encoding nucleic acid.
