שיטות ותכשירים לטיפול במחלת פברי
- 专利权人:
- SANGAMO THERAPEUTICS INC.
- 发明人:
- 申请号：
- IL26604719
- 公开号：
- IL266047D0
- 申请日:
- 2019.04.15
- 申请国别(地区):
- IL
- 年份:
- 2019
- 代理人:
- 摘要：
- Nucleases and methods of using these nucleases for inserting a sequence encoding a therapeutic α-Gal A protein such as an enzyme into a cell, thereby providing proteins or cell therapeutics for treatment and/or prevention of Fabry disease.
- 来源网站：
- 中国工程科技知识中心
相关发明人
相关专利
- Method of treating lysosomal storage diseases
- METHODS OF TREATING LYSOSOMAL STORAGE DISEASES
- A composition comprising Progranulin for preventing or treating liver disease
- Inhibitors of Furin and other pro-protein convertases
- SELF REMEDY SERVICE SYSTEM THROUGH THE EAR MASSAGE USING MOBILE PHONE AND METHOD THEREOF
