GUILD, Braydon, Charles,DEROSA, Frank,HEARTLEIN, Michael
申请号:
DK12728007
公开号:
DK2717893T3
申请日:
2012.06.08
申请国别(地区):
DK
年份:
2019
代理人:
摘要:
Disclosed herein are compositions and methods for modulating the production of a protein in a target cell. The compositions and methods disclosed herein are capable of ameliorating diseases associated with protein or enzyme deficiencies.