Methods and compositions for the treatment of neurologic disease

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专利权人:

REGENTS OF THE UNIVERSITY OF MINNESOTA

发明人:

申请号：

IL26035218

公开号：

IL260352D0

申请日:

2018.07.01

申请国别(地区):

IL

年份:

2018

代理人:

摘要：

Nucleases and methods of using these nucleases for inserting a sequence encoding a therapeutic IDUA or IDS protein such as an enzyme into a cell, thereby providing proteins or cell therapeutics for treatment and/or prevention of MPS I or MPS II disease.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/