LEONARD, JOHN P.,DELEUZE, JEAN-FRANCOIS,ITIER, JEAN-MICHEL,ORSINI, CECILE,RET-LECUELLE, GWENAELLE,VIALE, SANDRA
申请号：
CA2931981
公开号：
CA2931981A1
申请日:
2014.12.09
申请国别(地区):
CA
年份:
2015
代理人:
摘要：
The invention relates to inhibitors of glucosylceramide synthase (GCS) useful for the treatment metabolic diseases, such as lysosomal storage diseases, either alone or in combination with enzyme replacement therapy.
