RNA-modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders

• 收藏
• 分享

专利权人:

BIOMARIN TECHNOLOGIES B.V;BIOMARIN TECHNOLOGIES B.V.

发明人:

PETER CHRISTIAN DE VISSER,SUSAN ALLEGONDA MARIA MULDERS

申请号：

BR112014026285

公开号：

BR112014026285A8

申请日:

2013.04.23

申请国别(地区):

BR

年份:

2018

代理人:

摘要：

The current invention provides an improved oligonucleotide and its use for treating, ameliorating, preventing, delaying and/or treating a human cis-element repeat instability associated genetic neuromuscular or neurodegenerative disorder.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/