RNA modulating oligonucleotides with improved properties for the treatment of neuromuscular diseases

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专利权人:

BioMarin Technologies B.V.

发明人:

DE VISSER, Peter Christian,MULDERS, Susan Allegonda Maria

申请号：

DK13720617

公开号：

DK2841578T3

申请日:

2013.04.23

申请国别(地区):

DK

年份:

2017

代理人:

摘要：

The current invention provides an improved oligonucleotide and its use for treating, ameliorating, preventing, delaying and/or treating a human cis-element repeat instability associated genetic neuromuscular or neurodegenerative disorder.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/