exon jump compositions for treating muscular dystrophy

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专利权人:

SAREPTA THERAPEUTICS; INC.

发明人:

DIANE ELIZABETH FRANK,RICHARD K. BESTWICK

申请号：

BR112015023038

公开号：

BR112015023038A2

申请日:

2014.03.14

申请国别(地区):

BR

年份:

2017

代理人:

摘要：

abstract "exon bounce compositions for treating muscular dystrophy" antisense molecules capable of binding to a selected target site in the daistrofna huan gene to induce exon bounce 53 are described.resumo “composições para salto de exon para o tratamento da distrofia muscular” moléculas antissenso capazes de se ligarem a um sítio alvo selecionado no gene daistrofna huanapara induzir o salto do exon 53 são descritas.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/