EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
- 专利权人:
- Sarepta Therapeutics; Inc.
- 发明人:
- Richard K. Bestwick,Diane Elizabeth Frank
- 申请号：
- US14942629
- 公开号：
- US20160298111A1
- 申请日:
- 2015.11.16
- 申请国别(地区):
- US
- 年份:
- 2016
- 代理人:
- 摘要：
- Antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon 44 skipping are described.
- 来源网站：
- 中国工程科技知识中心
