COMPOSITIONS ET VARIANTS DE VIRUS ADÉNO-ASSOCIÉS ET PROCÉDÉS ET UTILISATIONS POUR UN TRANSFERT DE GÈNES DANS DES CELLULES, DES ORGANES ET DES TISSUS

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专利权人:

The Children's Hospital of Philadelphia

发明人:

申请号：

EP19197005.2

公开号：

EP3613440A1

申请日:

2014.07.22

申请国别(地区):

EP

年份:

2020

代理人:

摘要：

The invention relates to adeno-associated virus (AAV) serotype AAV-Rh74 and related AAV vectors, and AAV-Rh74 and related AAV vector mediated gene transfer methods and uses. In particular, AAV-Rh74 and related AAV vectors target polynucleotides to cells, tissues or organs for expression (transcription) of genes encoding therapeutic proteins and peptides, and polynucleotides that function as or are transcribed into inhibitory nucleic acid sequences.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/