CONSTRUCTIONS D'EXPRESSION DE FRATAXINE
- 专利权人:
- INTREXON CORPORATION
- 发明人:
- SCHAUER, STEPHEN,THOMAS, DARBY,ROBINSON, GREGORY,PYKETT, MARK,THORN, RICHARD,GRUIS, KIRSTEN
- 申请号:
- CA3042706
- 公开号:
- CA3042706A1
- 申请日:
- 2017.11.08
- 申请国别(地区):
- CA
- 年份:
- 2018
- 代理人:
- 摘要:
- The invention provides polynucleotides, vectors and viruses expressing frataxin and methods of treating Friedreich's Ataxia.
- 来源网站:
- 中国工程科技知识中心